Gene Therapy

Artificial intelligence-guided design of lipid nanoparticles for pulmonary gene therapy featured image

Artificial intelligence-guided design of lipid nanoparticles for pulmonary gene therapy

Deep learning framework (LiON) screens millions of lipid structures to identify novel nanoparticles for lung gene therapy. Cover article.

j.-witten

Combinatorial development of nebulized mRNA delivery formulations for the lungs

Combinatorial approach to develop nebulized mRNA delivery to the lungs.

j.-witten